Cell and Gene Therapies for Mucopolysaccharidoses: Base Editing and Therapeutic Delivery to the CNS

Diseases
doi 10.3390/diseases7030047
Full Text
Abstract

Available in full text

Date
Authors
Publisher

MDPI AG

Related search

Therapeutic Gene Editing: Delivery and Regulatory Perspectives

Acta Pharmacologica Sinica
MedicinePharmacology
2017English

Gene Editing for Advanced Therapies

OECD Science, Technology and Industry Working Papers
2018English

Viral Vectors and Delivery Strategies for CNS Gene Therapy

Therapeutic Delivery
Pharmaceutical Science
2010English

Delivery of CRISPR/Cas9 for Therapeutic Genome Editing

Journal of Gene Medicine
Molecular MedicineDrug DiscoveryGeneticsMolecular Biology
2019English

Cell Therapies for Therapeutic Angiogenesis: Back to the Bench

Vascular Medicine
MedicineCardiovascular MedicineCardiology
2009English

Bioreducible Polymers for Therapeutic Gene Delivery

Journal of Controlled Release
Pharmaceutical Science
2014English

Gene Delivery Technologies for Efficient Genome Editing: Applications in Gene Therapy

2016English

Cell and Gene Therapies: Moving From Research to Clinic

Journal of Translational Medicine
BiochemistryMedicineGeneticsMolecular Biology
2010English

TRAIL-based Gene Delivery and Therapeutic Strategies

Acta Pharmacologica Sinica
MedicinePharmacology
2019English

Amanote Research

Note-taking for researchers

Follow Amanote

© 2025 Amaplex Software S.P.R.L. All rights reserved.

Privacy PolicyRefund Policy