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mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency

Molecular Therapy - United States
doi 10.1016/j.ymthe.2019.04.017
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Abstract

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Categories
Molecular MedicineMolecular BiologyPharmacologyMedicineGeneticsDrug Discovery
Date

July 1, 2019

Authors
Jingsong CaoDing AnMikel GaldurozJenny ZhuoShi LiangMarianne EybyeAndrea FrassettoEishi KurodaAki FunahashiJordan SantanaCosmin MihaiKerry E. BenenatoE. Sathyajith KumarasingheStaci SabnisTimothy SalernoKimberly CoughlanEdward J. MiraccoBecca LevyGilles BesinJoshua SchultzChristine LukacsLin GueyPatrick FinnTatsuhiko FurukawaPaloma H. GiangrandeTakeyori SahekiPaolo G.V. Martini
Publisher

Elsevier BV

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