(PDF) 659. Development of an Effective AAV Vector-Based

659. Development of an Effective AAV Vector-Based Gene Therapy to Treat the PRKAG2-Tg Mice, an Animal Model of Autosomal Dominant Progressive Cardiomyopathy

Molecular Therapy - United States

doi 10.1016/s1525-0016(16)37232-x

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Date

May 1, 2011

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Unknown

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Elsevier BV

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659. Development of an Effective AAV Vector-Based Gene Therapy to Treat the PRKAG2-Tg Mice, an Animal Model of Autosomal Dominant Progressive Cardiomyopathy

Molecular Therapy - United States

doi 10.1016/s1525-0016(16)37232-x

Full Text

Abstract

Categories

Date

Authors

Publisher

Related search

159. Long-Term Rescue by AAV-Delivered Therapy in Autosomal Dominant Retinitis Pigmentosa (ADRP) Mice

Gene Mapping of Familial Autosomal Dominant Dilated Cardiomyopathy to Chromosome 10q21-23.

379 KB105: An HSV-based Gene Therapy Vector Engineered to Deliver Functional TGM1 to Autosomal Recessive Congenital Ichthyosis (ARCI) Keratinocytes

383 Preclinical Safety and Pharmacology of KB105, an HSV-based Gene Therapy Vector for the Treatment of Autosomal Recessive Congenital Ichthyosis (ARCI)

An AAV-derived Apaf-1 Dominant Negative Inhibitor Prevents MPTP Toxicity as Antiapoptotic Gene Therapy for Parkinson's Disease

The Search for an Effective Therapy to Treat Fragile X Syndrome: Dream or Reality?

A Gene for Fluctuating, Progressive Autosomal Dominant Nonsyndromic Hearing Loss, DFNA16, Maps to Chromosome 2q23-24.3

SRD005825 Acts as a Pharmacologic Chaperone of Opsin and Promotes Survival of Photoreceptors in an Animal Model of Autosomal Dominant Retinitis Pigmentosa

AAV Delivery of Wild-Type Rhodopsin Preserves Retinal Function in a Mouse Model of Autosomal Dominant Retinitis Pigmentosa