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197. AAV2/5-Mediated Gene Therapy Synergizes With Bone Marrow Transplantation in the Treatment of Infantile Neuronal Ceroid Lipofuscinosis
Molecular Therapy
- United States
doi 10.1016/s1525-0016(16)36769-7
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Abstract
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Categories
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Date
May 1, 2011
Authors
Unknown
Publisher
Elsevier BV
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