Correcting Neuromuscular Deficits With Gene Therapy in Pompe Disease

Annals of Neurology - United States
doi 10.1002/ana.24433
Full Text
Abstract

Available in full text

Categories
Neurology
Date
Authors
Publisher

Wiley

Related search

PHP7 Recent Developments in Pompe Disease Therapy

Value in Health
MedicineHealth PolicyPublic HealthOccupational HealthEnvironmental
2012English

Assessment of Toxicity and Biodistribution of Recombinant AAV8 Vector–mediated Immunomodulatory Gene Therapy in Mice With Pompe Disease

Molecular Therapy - Methods and Clinical Development
Molecular MedicineGeneticsMolecular Biology
2019English

Enzyme Replacement Therapy for Late-Onset Pompe Disease

Cochrane Database of Systematic Reviews
2018English

Pompe Disease

Neurologic Clinics
Neurology
2014English

Cost-Effectiveness of Enzyme Replacement Therapy With Alglucosidase Alfa in Adult Patients With Pompe Disease

Orphanet Journal of Rare Diseases
MedicineGeneticsPharmacology
2017English

Antisense Oligonucleotide Gene Therapy for Neuromuscular Disorders

University of Ottawa Journal of Medicine
2018English

Improvement of Dysphagia in a Child Affected by Pompe Disease Treated With Enzyme Replacement Therapy

Italian Journal of Pediatrics
Child HealthPediatricsPerinatology
2013English

Late-Onset Pompe Disease: Preliminary Results of Enzyme Replacement Therapy

Nervno-Myshechnye Bolezni
Neurology
2019English

Survival and Associated Factors in 268 Adults With Pompe Disease Prior to Treatment With Enzyme Replacement Therapy

Orphanet Journal of Rare Diseases
MedicineGeneticsPharmacology
2011English

Amanote Research

Note-taking for researchers

Follow Amanote

© 2024 Amaplex Software S.P.R.L. All rights reserved.

Privacy PolicyRefund Policy