Morpholino-Mediated Knockdown of DUX4 Toward Facioscapulohumeral Muscular Dystrophy Therapeutics
Molecular Therapy- United States
doi 10.1038/mt.2016.111
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Date
August 1, 2016
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Elsevier BV
doi 10.1038/mt.2016.111
Available in
August 1, 2016
Elsevier BV