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677. A Combination of Pharmacological and Liver-Directed Gene Therapy Results in Long-Term Phenotypic Correction of a Mouse Model of Argininosuccinic Aciduria
Molecular Therapy
- United States
doi 10.1016/s1525-0016(16)38118-7
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Categories
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Date
May 1, 2010
Authors
Unknown
Publisher
Elsevier BV
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