(PDF) Molecular Characterization of Mutations That Cause

Molecular Characterization of Mutations That Cause Globoid Cell Leukodystrophy and Pharmacological Rescue Using Small Molecule Chemical Chaperones

Journal of Neuroscience - United States

doi 10.1523/jneurosci.6383-09.2010

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April 21, 2010

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Society for Neuroscience

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