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Safety and Early Efficacy Outcomes for Lentiviral Fibroblast Gene Therapy in Recessive Dystrophic Epidermolysis Bullosa

JCI insight - United States
doi 10.1172/jci.insight.126243
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Abstract

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Categories
Medicine
Date

June 6, 2019

Authors
Su M. LwinFarhatullah SyedWei-Li DiTendai KadiyirireLu LiuAlyson GuyAnastasia PetrovaAlya Abdul-WahabFiona ReidRachel PhillipsMaria ElstadChristos GeorgiadisSophia AristodemouPatricia A. LovellJames R. McMillanJohn MeeSnaigune MiskinyteMatthias TiteuxLinda OzoemenaRashida PramanikSonia SerranoRacheal RowlesClarisse MaurinElizabeth OrrinMagdalena Martinez-QueipoEllie RashidghamatChristos TziotziosAlexandros OnoufriadisMei ChenLucas ChanFarzin FarzanehMarcela Del RioJakub TolarJohann W. BauerFernando LarcherMichael N. AntoniouAlain HovnanianAdrian J. ThrasherJemima E. MellerioWaseem QasimJohn A. McGrath
Publisher

American Society for Clinical Investigation

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