Amanote Research
Register
Sign In
880. Hematopoietic Stem Cell Gene Therapy for the Treatment of Metachromatic Leukodystrophy: Clinical Trial Design
Molecular Therapy
- United States
doi 10.1016/s1525-0016(16)40283-2
Full Text
Open PDF
Abstract
Available in
full text
Categories
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Date
May 1, 2008
Authors
Unknown
Publisher
Elsevier BV
Related search
Long-Term Outcomes After Allogeneic Hematopoietic Stem Cell Transplantation for Metachromatic Leukodystrophy: The Largest Single-Institution Cohort Report
Orphanet Journal of Rare Diseases
Medicine
Genetics
Pharmacology
Metachromatic Leukodystrophy
Challenges in Vector and Trial Design Using Retroviral Vectors for Long-Term Gene Correction in Hematopoietic Stem Cell Gene Therapy
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Hematopoietic-Stem-Cell-Based Gene Therapy for HIV Disease
Cell Stem Cell
Molecular Medicine
Genetics
Cell Biology
Reduced Intensity Conditioning Haematopoietic Stem Cell Transplantation With Mesenchymal Stromal Cells Infusion for the Treatment of Metachromatic Leukodystrophy: A Case Report
Haematologica
Hematology
Recent Advances in Hematopoietic Stem Cell Gene Therapy
Induced Transgene Expression for the Treatment of Solid Tumors by Hematopoietic Stem Cell-Based Gene Therapy
Cancer Gene Therapy
Cancer Research
Molecular Medicine
Molecular Biology
Oligodendroglial Progenitor Cell Therapy Limits Central Neurological Deficits in Mice With Metachromatic Leukodystrophy
Journal of Neuroscience
Neuroscience
Development of a Modified Selective Amplifier Gene for Hematopoietic Stem Cell Gene Therapy
Gene Therapy
Molecular Medicine
Genetics
Molecular Biology