Spliceosome-Mediated RNATrans-Splicing With Recombinant Adeno-Associated Virus Partially Restores Cystic Fibrosis Transmembrane Conductance Regulator Function to Polarized Human Cystic Fibrosis Airway Epithelial Cells

Human Gene Therapy - United States
doi 10.1089/hum.2005.16.1116