(PDF) 066 Avxs-101 Gene-Replacement Therapy (GRT) for

066 Avxs-101 Gene-Replacement Therapy (GRT) for Spinal Muscular Atrophy Type 1 (SMA1): Pivotal Phase 3 Study (STR1VE) Update

Journal of Neurology, Neurosurgery and Psychiatry - United Kingdom

doi 10.1136/jnnp-2019-anzan.58

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