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Publications by Fabio Candotti
30. Phase II Clinical Trial of Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA-SCID) Using a Γ-Retroviral Vector
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Human Adenylate Kinase 2 Deficiency Causes a Profound Hematopoietic Defect Associated With Sensorineural Deafness
Nature Genetics
Genetics
Lessons From the Wiskott–Aldrich Syndrome
New England Journal of Medicine
Medicine
Second-Site Mutation in the Wiskott-Aldrich Syndrome (WAS) Protein Gene Causes Somatic Mosaicism in Two WAS Siblings
Journal of Clinical Investigation
Medicine