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Publications by Harald Petry
Phase I Open Label Liver-Directed Gene Therapy Clinical Trial for Acute Intermittent Porphyria
Journal of Hepatology
Hepatology
546. Development of MFP-Inducible System for AAV5 Gene Therapy of Chronic Diseases in the Liver
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Design, Characterization, and Lead Selection of Therapeutic miRNAs Targeting Huntingtin for Development of Gene Therapy for Huntington's Disease
Molecular Therapy - Nucleic Acids
Drug Discovery
Molecular Medicine
Targeting RNA-mediated Toxicity in C9ORF72 ALS/FTD by RNAi-based Gene Therapy
Molecular Therapy - Nucleic Acids
Drug Discovery
Molecular Medicine
Optimization of Viral Protein Ratios for Production of rAAV Serotype 5 in the Baculovirus System
Gene Therapy
Molecular Medicine
Genetics
Molecular Biology
Long-Term Increased Carnitine Palmitoyltransferase 1A Expression in Ventromedial Hypotalamus Causes Hyperphagia and Alters the Hypothalamic Lipidomic Profile
PLoS ONE
Multidisciplinary
Optimization and Comparison of Knockdown Efficacy Between Polymerase II Expressed shRNA and Artificial miRNA Targeting Luciferase and Apolipoprotein B100
BMC Biotechnology
Biotechnology
Insect Cell-Based Recombinant Adeno-Associated Virus Production: Molecular Process Optimization
BioProcessing Journal
