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Publications by Janne J. Turunen
581. Correcting Exon Skipping Splicing Defects in BTK RNA by Using Bifunctional Oligonucleotides
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
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Splice-Correcting Oligonucleotides Restore BTK Function in X-Linked Agammaglobulinemia Model
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Ribozyme Stability, Exon Skipping, and a Potential Role for RNA Helicase in Group I Intron Splicing by Coxiella Burnetii
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Multiple Splicing Defects in an Intronic False Exon
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Dynamic ASXL1 Exon Skipping and Alternative Circular Splicing in Single Human Cells
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Thousands of Exon Skipping Events Differentiate Among Splicing Patterns in Sixteen Human Tissues
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Polyquaternium-Mediated Delivery of Morpholino Oligonucleotides for Exon-Skipping in Vitro and in MDX Mice
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Nucleobase-Modified Antisense Oligonucleotides Containing 5-(Phenyltriazol)-2′-Deoxyuridine Nucleotides Induce Exon-Skipping in Vitro
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Regulation of Alternative RNA Splicing by Exon Definition and Exon Sequences in Viral and Mammalian Gene Expression
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Wild-Type Mouse Models to Screen Antisense Oligonucleotides for Exon-Skipping Efficacy in Duchenne Muscular Dystrophy
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