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Publications by Maria Carmina Ferrara
Structure of Human Lysosomal Acid Α-Glucosidase–A Guide for the Treatment of Pompe Disease
Nature Communications
Astronomy
Genetics
Molecular Biology
Biochemistry
Chemistry
Physics
Related publications
Glycosylation-Independent Lysosomal Targeting of Acid Α-Glucosidase Enhances Muscle Glycogen Clearance in Pompe Mice
Journal of Biological Chemistry
Biochemistry
Cell Biology
Molecular Biology
618. Adjunctive Γ2-Agonist Therapy Enhances Trafficking of Acid Α-Glucosidase to Lysosomes in the Skeletal Muscle of Mice With Pompe Disease
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Discovery of a Novel Noniminosugar Acid Α Glucosidase Chaperone Series
Journal of Medicinal Chemistry
Drug Discovery
Molecular Medicine
Cloning, Expression, Purification, and Characterization of the Human Broad Specificity Lysosomal Acid Α-Mannosidase
Journal of Biological Chemistry
Biochemistry
Cell Biology
Molecular Biology
472. Evaluation of Re-Administration of a Recombinant Adeno-Associated Vector Expressing Acid-Alpha-Glucosidase (rAAV9-DES-hGAA) in Pompe Disease: Preclinical to Clinical Planning
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Differences in the Predominance of Lysosomal and Autophagic Pathologies Between Infants and Adults With Pompe Disease: Implications for Therapy
Molecular Genetics and Metabolism
Genetics
Molecular Biology
Biochemistry
Endocrinology
Metabolism
Diabetes
Pompe Disease
Neurologic Clinics
Neurology
Structure, Properties, and Tissue Localization of Apoplastic Α-Glucosidase in Crucifers
Plant Physiology
Plant Science
Genetics
Physiology
Wolman Disease/Cholesteryl Ester Storage Disease: Efficacy of Plant-Produced Human Lysosomal Acid Lipase in Mice
Journal of Lipid Research
Biochemistry
Endocrinology
Cell Biology
