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Publications by Melissa A. Goddard

Gene Therapy in Monogenic Congenital Myopathies

English

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Correction: Integrative Data Mining Highlights Candidate Genes for Monogenic Myopathies

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Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

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A Mutation Update for the FLNC Gene in Myopathies and Cardiomyopathies

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Characterization of an Animal Model for Congenital Myopathies Linked to Recessive RyR1 Mutations

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