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Publications by Miarasa S. Steele
A G542X Cystic Fibrosis Mouse Model for Examining Nonsense Mutation Directed Therapies
PLoS ONE
Multidisciplinary
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Severe Cystic Fibrosis in a Child Homozygous for the G542 Nonsense Mutation in the CFTR Gene.
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Nine Cystic Fibrosis Patients Homozygous for the CFTR Nonsense Mutation R1162X Have Mild or Moderate Lung Disease.
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Mouse as a Model of Growth Retardation in Cystic Fibrosis
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