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Publications by Michael Rotstein

Consideration of Gene Therapy for Paediatric Neurotransmitter Diseases

Journal of Inherited Metabolic Disease
Genetics
2009English

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Gene Therapy for Neurodegenerative Diseases

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Gene Therapy for CNS Diseases – Krabbe Disease

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Paediatric Diseases

Bone Marrow Transplantation
TransplantationHematology
2000English

Fetal Gene Therapy for Neurodegenerative Lysosomal Storage Diseases

Journal of Inherited Metabolic Disease
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2019English

RNAi-based Gene Therapy for Blood Genetic Diseases

2016English

Gene Therapy for Neurodegenerative Diseases: Fact or Fiction?

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2001English

Adeno-Associated Virus-Based Gene Therapy for CNS Diseases

Human Gene Therapy
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2016English

Gene Therapy for Rare Diseases – The Case for Acute Intermittent Porphyria

EPMA Journal
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2014English

309. Optimization of Dual AAV Vectors for Gene Therapy of Inherited Retinal Diseases

Molecular Therapy
Molecular MedicineMolecular BiologyPharmacologyMedicineGeneticsDrug Discovery
2015English

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