Amanote Research
Register
Sign In
Discover open access scientific publications
Search, annotate, share and cite publications
Publications by Miguel Sena-Esteves
Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Survival Benefit and Phenotypic Improvement by Hamartin Gene Therapy in a Tuberous Sclerosis Mouse Brain Model
Neurobiology of Disease
Neurology
Intracranial AAV-IFN-β Gene Therapy Eliminates Invasive Xenograft Glioblastoma and Improves Survival in Orthotopic Syngeneic Murine Model
Molecular Oncology
Cancer Research
Medicine
Oncology
Genetics
Molecular Medicine
Cerebral Organoids Derived From Sandhoff Disease Induced Pluripotent Stem Cells Exhibit Impaired Neurodifferentiation
Journal of Lipid Research
Biochemistry
Endocrinology
Cell Biology
Biomarkers for Disease Progression and AAV Therapeutic Efficacy in Feline Sandhoff Disease
Experimental Neurology
Developmental Neuroscience
Neurology
Adeno-Associated Virus Neutralizing Antibodies in Large Animals and Their Impact on Brain Intraparenchymal Gene Transfer
Molecular Therapy - Methods and Clinical Development
Molecular Medicine
Genetics
Molecular Biology
GaussiaLuciferase Variant for High-Throughput Functional Screening Applications
Analytical Chemistry
Analytical Chemistry
