Amanote Research
Register
Sign In
Discover open access scientific publications
Search, annotate, share and cite publications
Publications by Monique MA Verstegen
Correction of Murine SCID-X1 by Lentiviral Gene Therapy Using a Codon-Optimized IL2RG Gene and Minimal Pretransplant Conditioning
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Related publications
Gene Correction for SCID-X1 in Long-Term Hematopoietic Stem Cells
Nature Communications
Astronomy
Genetics
Molecular Biology
Biochemistry
Chemistry
Physics
Preclinical Development of Gene Therapy for X-Linked Severe Combined Immunodeficiency (SCID-X1)
Blood
Biochemistry
Immunology
Cell Biology
Hematology
Improvement of Bone and Dental Phenotype of Murine Hypophosphatasia Mediated by a Single Injection of Lentiviral Gene Therapy
Open Journal of Stomatology
Correction of B-Cell Development in BTK-Deficient Mice Using Lentiviral Vectors With Codon-Optimized Human BTK
Leukemia
Cancer Research
Oncology
Anesthesiology
Pain Medicine
Hematology
Optimized Lentiviral Vectors for HIV Gene Therapy: Multiplexed Expression of Small RNAs and Inclusion of MGMTP140K Drug Resistance Gene
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
310. Comparison of Integration Site Profiles Between SCID-X1 Gene Therapy Trials Using Gammaretroviral Vectors With Intact or Deleted (SIN) LTRs
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
93. Generation of Gene-Corrected, Vector- And Reprogramming Factor-Free iPS Cells From SCID-X1 Patients
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Gene Replacement of IL2RG for SCID Defect Associated With Increased Risk of Lymphoma in Mice
Cancer Biology and Therapy
Cancer Research
Oncology
Molecular Medicine
Pharmacology
Lentiviral Gene Therapy Vectors: Challenges and Future Directions