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Publications by Natalia V. Zhurkova
Mucopolysaccharidosis Type II: Enzyme Replacement Therapy Efficiency
Voprosy Sovremennoi Pediatrii - Current Pediatrics
Child Health
Pediatrics
Perinatology
The Urgency of Genetic Verification of Non-Compaction Cardiomyopathy in Children: Clinical Cases
Voprosy Sovremennoi Pediatrii - Current Pediatrics
Child Health
Pediatrics
Perinatology
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Pharmacoeconomic Evaluation of Drugs Used in Enzyme Replacement Therapy Mucopolysaccharidosis Type II
Pharmacoeconomics: theory and practice
Limited Data to Evaluate Real‐World Effectiveness of Enzyme Replacement Therapy for Mucopolysaccharidosis Type I
Journal of Inherited Metabolic Disease
Genetics
Immune Response to Intrathecal Enzyme Replacement Therapy in Mucopolysaccharidosis I Patients
Pediatric Research
Child Health
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Perinatology
Enzyme Replacement Therapy Treatment From Birth Increases Therapeutic Efficacy and Generates Tolerance to Enzyme in Canine Mucopolysaccharidosis Type I
Monitoring Dose Response of Enzyme Replacement Therapy in Feline Mucopolysaccharidosis Type VI by Tandem Mass Spectrometry
Pediatric Research
Child Health
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Enzyme Replacement With Recombinant Β-Glucuronidase in the Newborn Mucopolysaccharidosis Type VII Mouse
Pediatric Research
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Perinatology
Effects of Neonatal Enzyme Replacement Therapy and Simvastatin Treatment on Cervical Spine Disease in Mucopolysaccharidosis I Dogs
Journal of Bone and Mineral Research
Endocrinology
Orthopedics
Sports Medicine
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Cost-Effectiveness of Enzyme Replacement Therapy for Type 1 Gaucher Disease
Orphanet Journal of Rare Diseases
Medicine
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Pharmacology
Laronidase Replacement Therapy and Left Ventricular Function in Mucopolysaccharidosis I
JIMD Reports
Internal Medicine
Genetics
Molecular Biology
Biochemistry
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Metabolism
Diabetes