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Publications by Paul A Sieving
Ocular and Systemic Safety of a Recombinant AAV8 Vector for X-Linked Retinoschisis Gene Therapy: GLP Studies in Rabbits and Rs1-Ko Mice
Molecular Therapy - Methods and Clinical Development
Molecular Medicine
Genetics
Molecular Biology
Related publications
Preclinical Safety Evaluation of a Recombinant AAV8 Vector for X-Linked Retinoschisis After Intravitreal Administration in Rabbits
Human gene therapy. Clinical development
Genetics
Systemic Safety of a Recombinant AAV8 Vector for Human Cocaine Hydrolase Gene Therapy: A Good Laboratory Practice Preclinical Study in Mice
Human Gene Therapy
Molecular Medicine
Genetics
Molecular Biology
Assessment of Toxicity and Biodistribution of Recombinant AAV8 Vector–mediated Immunomodulatory Gene Therapy in Mice With Pompe Disease
Molecular Therapy - Methods and Clinical Development
Molecular Medicine
Genetics
Molecular Biology
Multimodal Imaging in a Pedigree of X-Linked Retinoschisis With a Novel RS1 Variant
BMC Medical Genetics
Genetics
Cog-Wheel Octameric Structure of RS1, the Discoidin Domain Containing Retinal Protein Associated With X-Linked Retinoschisis
PLoS ONE
Multidisciplinary
Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatosis
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
174. Liver Fibrosis in Aged OTC-KO Heterozygotes and Successful Correction by AAV8-Mediated Gene Therapy
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Bullous X Linked Retinoschisis: Clinical Features and Prognosis
British Journal of Ophthalmology
Molecular Neuroscience
Ophthalmology
Sensory Systems
Cellular
Retinal Function in X-Linked Juvenile Retinoschisis
Investigative Ophthalmology and Visual Science
Molecular Neuroscience
Ophthalmology
Sensory Systems
Cellular
