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Publications by R Richardson

B.06 Safety and Efficacy of Nusinersen in Infants/Children With Spinal Muscular Atrophy (SMA): Part 1 of the Phase 2 EMBRACE Study

Canadian Journal of Neurological Sciences

English

Etaii 6 Mev Pepperpot Emittance Measurement

English

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Cost of Illness of Spinal Muscular Atrophy (SMA) in Italy

Global and Regional Health Technology Assessment

English

Spinal Muscular Atrophy Type 1

Pediatric Critical Care Medicine

Intensive Care Medicine

English

Efficacy and Safety of Dutasteride in Patients With Spinal and Bulbar Muscular Atrophy: A Randomised Placebo-Controlled Trial

The Lancet Neurology

English

NCALD Antisense Oligonucleotide Therapy in Addition to Nusinersen Further Ameliorates Spinal Muscular Atrophy in Mice

American Journal of Human Genetics

English

Respiratory Management of the Infant With Type 1 Spinal Muscular Atrophy

Archives of Disease in Childhood

English

ECG in Neonate Mice With Spinal Muscular Atrophy Allows Assessment of Drug Efficacy

Frontiers in Bioscience - Elite

Molecular Biology

English

014 AVXS-101 Gene-Replacement Therapy (GRT) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update

Journal of Neurology, Neurosurgery and Psychiatry

English

P.065 AVXS-101 Gene-Replacement Therapy (GRT)) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update

Canadian Journal of Neurological Sciences

English

Reliability of the Modified Hammersmith Functional Motor Scale in Young Children With Spinal Muscular Atrophy

Muscle and Nerve

Molecular Neuroscience

English