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Publications by Sandra H van Heiningen
Dual Exon Skipping in Myostatin and Dystrophin for Duchenne Muscular Dystrophy
BMC Medical Genomics
Genetics
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Exon Skipping: A First in Class Strategy for Duchenne Muscular Dystrophy
Expert Opinion on Biological Therapy
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Intravenous Infusion of an Antisense Oligonucleotide Results in Exon Skipping in Muscle Dystrophin mRNA of Duchenne Muscular Dystrophy
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Child Health
Pediatrics
Perinatology
Efficacy of Multi-Exon Skipping Treatment in Duchenne Muscular Dystrophy Dog Model Neonates
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Antisense Oligo-Mediated Multiple Exon Skipping in a Dog Model of Duchenne Muscular Dystrophy
Methods in Molecular Biology
Genetics
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Wild-Type Mouse Models to Screen Antisense Oligonucleotides for Exon-Skipping Efficacy in Duchenne Muscular Dystrophy
PLoS ONE
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Autoimmune Response and Its Long‐term Consequences After Exon‐skipping Therapy in a Duchenne Muscular Dystrophy Mouse Model
Journal of Pathology
Forensic Medicine
Pathology
Prednisolone Treatment Does Not Interfere With 2′-O-Methyl Phosphorothioate Antisense-Mediated Exon Skipping in Duchenne Muscular Dystrophy
Human Gene Therapy
Molecular Medicine
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Immune Responses to Dystrophin: Implications for Gene Therapy of Duchenne Muscular Dystrophy
Gene Therapy
Molecular Medicine
Genetics
Molecular Biology
A Multicenter Comparison of Quantification Methods for Antisense Oligonucleotide-Induced DMD Exon 51 Skipping in Duchenne Muscular Dystrophy Cell Cultures
PLoS ONE
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