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Publications by T. E. Bertorini
Randomized, Blinded Trial of Weekend vs Daily Prednisone in Duchenne Muscular Dystrophy
Neurology
Neurology
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Duchenne Muscular Dystrophy
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Methods in Molecular Biology
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Duchenne Muscular Dystrophy
Risks in a Trial of an Innovative Treatment of Duchenne Muscular Dystrophy
Pediatrics
Child Health
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Bladder Dysfunction in Duchenne Muscular Dystrophy
Archives of Disease in Childhood
Child Health
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Airway Clearance in Duchenne Muscular Dystrophy
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Placebo-Controlled Phase 2 Trial of Drisapersen for Duchenne Muscular Dystrophy
Annals of Clinical and Translational Neurology
Neuroscience
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150. Ex Vivo Gene Therapy of Duchenne Muscular Dystrophy Using iPSCs From Duchenne Muscular Dystrophy Patients
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Pharmacology
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Drug Discovery