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Publications by Terence R. Flotte
Results at 2 Years After Gene Therapy for RPE65-Deficient Leber Congenital Amaurosis and Severe Early-Childhood–Onset Retinal Dystrophy
Ophthalmology
Ophthalmology
Adeno-Associated Virus Neutralizing Antibodies in Large Animals and Their Impact on Brain Intraparenchymal Gene Transfer
Molecular Therapy - Methods and Clinical Development
Molecular Medicine
Genetics
Molecular Biology
Characterization of a Recombinant Adeno-Associated Virus Type 2 Reference Standard Material
Human Gene Therapy
Molecular Medicine
Genetics
Molecular Biology
No Immune Responses by the Expression of the Yeast Ndi1 Protein in Rats
PLoS ONE
Multidisciplinary
Gene Transfer in the Lung Using Recombinant Adeno-Associated Virus
Current Protocols in Microbiology
Medicine
Virology
Parasitology
Microbiology
Gene Transfer in Skeletal and Cardiac Muscle Using Recombinant Adeno-Associated Virus
Current Protocols in Microbiology
Medicine
Virology
Parasitology
Microbiology
Use of the NADH-Quinone Oxidoreductase (NDI1) Gene ofSaccharomyces Cerevisiaeas a Possible Cure for Complex I Defects in Human Cells
Journal of Biological Chemistry
Biochemistry
Cell Biology
Molecular Biology
Treatment of Leber Congenital Amaurosis Due toRPE65Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial
Human Gene Therapy
Molecular Medicine
Genetics
Molecular Biology
Biochemical Correction of Short-Chain Acyl-Coenzyme a Dehydrogenase Deficiency After Portal Vein Injection of rAAV8-SCAD
Human Gene Therapy
Molecular Medicine
Genetics
Molecular Biology
