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Publications by William W. Hauswirth
Results at 2 Years After Gene Therapy for RPE65-Deficient Leber Congenital Amaurosis and Severe Early-Childhood–Onset Retinal Dystrophy
Ophthalmology
Ophthalmology
299. Safety and Biodistribution Study of rAAV2tYF-PR1.7-hCNGB3 in CNGB3-Deficient Mice
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
599. Deep Informatics Utilized to Design MiniPromoters for Driving PAX6-Like Retinal Expression With AAV
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Organizational Motifs for Ground Squirrel Cone Bipolar Cells
Journal of Comparative Neurology
Neuroscience
Cone Phosphodiesterase-6γ’ Subunit Augments Cone PDE6 Holoenzyme Assembly and Stability in a Mouse Model Lacking Both Rod and Cone PDE6 Catalytic Subunits
Frontiers in Molecular Neuroscience
Molecular Neuroscience
Molecular Biology
Cellular
XIAP Therapy Increases Survival of Transplanted Rod Precursors in a Degenerating Host Retina
Investigative Ophthalmology and Visual Science
Molecular Neuroscience
Ophthalmology
Sensory Systems
Cellular
AAV Delivery of Wild-Type Rhodopsin Preserves Retinal Function in a Mouse Model of Autosomal Dominant Retinitis Pigmentosa
Human Gene Therapy
Molecular Medicine
Genetics
Molecular Biology
Ab-Externo AAV-Mediated Gene Delivery to the Suprachoroidal Space Using a 250 Micron Flexible Microcatheter
PLoS ONE
Multidisciplinary
RNAi-Mediated Gene Suppression in a GCAP1(L151F) Cone-Rod Dystrophy Mouse Model
PLoS ONE
Multidisciplinary
Safety and Biodistribution Evaluation in Cynomolgus Macaques of rAAV2tYF-PR1.7-hCNGB3, a Recombinant AAV Vector for Treatment of Achromatopsia
Human gene therapy. Clinical development
Genetics
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