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Publications in Molecular Medicine

Improved Survival and Reduced Phenotypic Severity Following AAV9/MECP2 Gene Transfer to Neonatal and Juvenile Male Mecp2 Knockout Mice

Molecular Therapy

English

507. Transcriptional Repression of the Rhodopsin Gene via Zinc-Finger Technology for the Treatment of the Dominant Retinal Degenerations

English

372. Prevalence of Anti-Aav8 Neutralizing Antibodies and ARSB Cross-Reactive Immunologic Material in MPS VI Patients Candidates for a Gene Therapy Trial

English

594. PEGylated Polyacridine-Peptide DNA Open-Polyplexes With Long Pharmacokinetic Half-Life Have Improved Hydrodynamic Stimulated Gene Expression

English

545. Highly Efficient Tumor Transduction and Antitumor Efficacy in Experimental Human Malignant Mesothelioma Using Replicating Gibbon Ape Leukemia Virus

English

Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatosis

English

124. AAV-Mediated Antisense Oligonucleotide-Based Therapy for CEP290-Associated LCA

English

137. Viral Hitchhiking to Increase Therapeutic Potential: Autonomously Packaged Elements (APEs)

English

635. Development of Plasmid-Lipoparticle Systemic Delivery System That Overcome the Paradox of PEG-Stabilization While Maintaining High Transfection Potency

English

481. Analysis of Host Cell and Viral Transcriptomes During Infection by Wild-Type Species C Ad6 and Species D Ad26

English

Amanote Research

Discover open access scientific publications

Search, annotate, share and cite publications

Publications in Molecular Medicine

Improved Survival and Reduced Phenotypic Severity Following AAV9/MECP2 Gene Transfer to Neonatal and Juvenile Male Mecp2 Knockout Mice

507. Transcriptional Repression of the Rhodopsin Gene via Zinc-Finger Technology for the Treatment of the Dominant Retinal Degenerations

372. Prevalence of Anti-Aav8 Neutralizing Antibodies and ARSB Cross-Reactive Immunologic Material in MPS VI Patients Candidates for a Gene Therapy Trial

594. PEGylated Polyacridine-Peptide DNA Open-Polyplexes With Long Pharmacokinetic Half-Life Have Improved Hydrodynamic Stimulated Gene Expression

545. Highly Efficient Tumor Transduction and Antitumor Efficacy in Experimental Human Malignant Mesothelioma Using Replicating Gibbon Ape Leukemia Virus

Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatosis

124. AAV-Mediated Antisense Oligonucleotide-Based Therapy for CEP290-Associated LCA

137. Viral Hitchhiking to Increase Therapeutic Potential: Autonomously Packaged Elements (APEs)

635. Development of Plasmid-Lipoparticle Systemic Delivery System That Overcome the Paradox of PEG-Stabilization While Maintaining High Transfection Potency

481. Analysis of Host Cell and Viral Transcriptomes During Infection by Wild-Type Species C Ad6 and Species D Ad26