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Publications in Molecular Medicine

The Impact of Minimally Oversized Adeno-Associated Viral Vectors Encoding Human Factor VIII on Vector Potency in Vivo

Molecular Therapy - Methods and Clinical Development

English

Amino Acid and Small GTPase Regulation of mTORC1

English

Genetic Engineering of T Cells for Immune Tolerance

Molecular Therapy - Methods and Clinical Development

English

In Silico Restriction Enzyme Digests to Minimize Mapping Bias in Genomic Sequencing

Molecular Therapy - Methods and Clinical Development

English

Genome Editing in Patient iPSC Efficiently Corrects the Most Prevalent USH2A Mutations and Reveals Intriguing Mutant mRNA Expression Profiles

Molecular Therapy - Methods and Clinical Development

English

Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice With Mutations in the FKRP Gene

Molecular Therapy - Methods and Clinical Development

English

Putative Terminator and/or Effector Functions of Arf GAPs in the Trafficking of Clathrin-Coated Vesicles

English

Phase 1 Safety and Immunogenicity Trial of Recombinant Lactococcus Lactis Expressing Human Papillomavirus Type 16 E6 Oncoprotein Vaccine in Healthy Females

Molecular Therapy - Methods and Clinical Development

English

Immune Modulatory Cell Therapy for Hemophilia B Based on CD20-Targeted Lentiviral Gene Transfer to Primary B Cells

Molecular Therapy - Methods and Clinical Development

English

Advancements and Obstacles of CRISPR-Cas9 Technology in Translational Research

Molecular Therapy - Methods and Clinical Development

English

Amanote Research

Discover open access scientific publications

Search, annotate, share and cite publications

Publications in Molecular Medicine

The Impact of Minimally Oversized Adeno-Associated Viral Vectors Encoding Human Factor VIII on Vector Potency in Vivo

Amino Acid and Small GTPase Regulation of mTORC1

Genetic Engineering of T Cells for Immune Tolerance

In Silico Restriction Enzyme Digests to Minimize Mapping Bias in Genomic Sequencing

Genome Editing in Patient iPSC Efficiently Corrects the Most Prevalent USH2A Mutations and Reveals Intriguing Mutant mRNA Expression Profiles

Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice With Mutations in the FKRP Gene

Putative Terminator and/or Effector Functions of Arf GAPs in the Trafficking of Clathrin-Coated Vesicles

Phase 1 Safety and Immunogenicity Trial of Recombinant Lactococcus Lactis Expressing Human Papillomavirus Type 16 E6 Oncoprotein Vaccine in Healthy Females

Immune Modulatory Cell Therapy for Hemophilia B Based on CD20-Targeted Lentiviral Gene Transfer to Primary B Cells

Advancements and Obstacles of CRISPR-Cas9 Technology in Translational Research