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288. Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatous Disease

Molecular Therapy - United States
doi 10.1016/s1525-0016(16)33897-7
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Abstract

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Categories
Molecular MedicineMolecular BiologyPharmacologyMedicineGeneticsDrug Discovery
Date

May 1, 2015

Authors
Giada FarinelliMaria ChiriacoValentina CapoErika ZonariMaddalena MigliavaccaRaisa Jofra HernandezSamantha ScaramuzzaGigliola Di MatteoLucia Sergi SergiAlice RossiSerena RanucciAlessandra BragonziAnna Kajaste-RudnitskiDidier TronoManuel GrezPaolo RossiAndrea FinocchiLuigi NaldiniBernhard GentnerAlessandro Aiuti
Publisher

Elsevier BV

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