Amanote Research
Register
Sign In
606. Restricting MTM1 Transgene Expression to Skeletal Muscle in AAV-Mediated Gene Therapy for Myotubular Myopathy
Molecular Therapy
- United States
doi 10.1016/s1525-0016(16)34941-3
Full Text
Open PDF
Abstract
Available in
full text
Categories
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Date
May 1, 2013
Authors
Unknown
Publisher
Elsevier BV
Related search
36. AAV-MTM1 Prolongs Survival and Rescues Severe Muscle Weakness in Mouse and Canine Models of X-Linked Myotubular Myopathy
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Improving AAV Gene Therapy: Graduating From Transgene Expression “Everywhere, All the Time” to “Disease-Specific”
Cloning & Transgenesis
Repression of Retrovirus-Mediated Transgene Expression by Interferons: Implications for Gene Therapy.
Journal of Virology
Insect Science
Immunology
Microbiology
Virology
a Novel Intronic Mutation in MTM1 Detected by RNA Analysis in a Case of X-Linked Myotubular Myopathy
Neurology: Genetics
Neurology
Genetics
402. Gait Function in a Canine Model of X-Linked Myotubular Myopathy After Systemic Delivery of AAV8-MTM1
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
A MicroRNA124 Target Sequence Restores Astrocyte Specificity of gfaABC 1 D-Driven Transgene Expression in AAV-Mediated Gene Transfer
Molecular Therapy - Nucleic Acids
Drug Discovery
Molecular Medicine
Targeted Expression of IGF-1 Transgene to Skeletal Muscle Accelerates Muscle and Motor Neuron Regeneration
FASEB Journal
Biochemistry
Biotechnology
Genetics
Molecular Biology
Medicine
AAV-mediated Gene Transfer for Hemophilia
Genetics in Medicine
Medicine
Genetics
Optimization of AAV Expression Cassettes to Improve Packaging Capacity and Transgene Expression in Neurons
Molecular Brain
Molecular Neuroscience
Molecular Biology
Cellular
