36. AAV-MTM1 Prolongs Survival and Rescues Severe Muscle Weakness in Mouse and Canine Models of X-Linked Myotubular Myopathy

Molecular Therapy - United States
doi 10.1016/s1525-0016(16)35840-3
Full Text
Abstract

Available in full text

Date
Authors

Unknown

Publisher

Elsevier BV

Related search

402. Gait Function in a Canine Model of X-Linked Myotubular Myopathy After Systemic Delivery of AAV8-MTM1

Molecular Therapy
Molecular MedicineMolecular BiologyPharmacologyMedicineGeneticsDrug Discovery
2014English

606. Restricting MTM1 Transgene Expression to Skeletal Muscle in AAV-Mediated Gene Therapy for Myotubular Myopathy

Molecular Therapy
Molecular MedicineMolecular BiologyPharmacologyMedicineGeneticsDrug Discovery
2013English

X-Linked Myotubular Myopathy-Abnormal Genitalia Syndrome

2020English

a Novel Intronic Mutation in MTM1 Detected by RNA Analysis in a Case of X-Linked Myotubular Myopathy

Neurology: Genetics
NeurologyGenetics
2017English

Reducing Dynamin 2 Expression Rescues X-Linked Centronuclear Myopathy

Journal of Clinical Investigation
Medicine
2014English

498. Prolonged Benefit From Systemic rAAV8 in a Canine Model of Myotubular Myopathy

Molecular Therapy
Molecular MedicineMolecular BiologyPharmacologyMedicineGeneticsDrug Discovery
2016English

Endoscopic Third Ventriculostomy With Choroid Plexus Coagulation for Treatment of Hydrocephalus in X-Linked Myotubular Myopathy: A Novel Approach

Cureus
2018English

Deletion of the Ste20-Like Kinase SLK in Skeletal Muscle Results in a Progressive Myopathy and Muscle Weakness

Skeletal Muscle
OrthopedicsSports MedicineCell BiologyMolecular Biology
2017English

Two Brothers With Very Late Onset of Muscle Weakness in X-Linked Recessive Spinal and Bulbar Muscular Atrophy

Clinical Neurology
Neurology
2009English

Amanote Research

Note-taking for researchers

Follow Amanote

© 2026 Amaplex Software S.P.R.L. All rights reserved.

Privacy PolicyRefund Policy