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Publications by Adrian G. Todd

Correcting Neuromuscular Deficits With Gene Therapy in Pompe Disease

Annals of Neurology
Neurology
2015English

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PHP7 Recent Developments in Pompe Disease Therapy

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Assessment of Toxicity and Biodistribution of Recombinant AAV8 Vector–mediated Immunomodulatory Gene Therapy in Mice With Pompe Disease

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Enzyme Replacement Therapy for Late-Onset Pompe Disease

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Cost-Effectiveness of Enzyme Replacement Therapy With Alglucosidase Alfa in Adult Patients With Pompe Disease

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Antisense Oligonucleotide Gene Therapy for Neuromuscular Disorders

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Improvement of Dysphagia in a Child Affected by Pompe Disease Treated With Enzyme Replacement Therapy

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Late-Onset Pompe Disease: Preliminary Results of Enzyme Replacement Therapy

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Survival and Associated Factors in 268 Adults With Pompe Disease Prior to Treatment With Enzyme Replacement Therapy

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