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Publications by Alessandro Aiuti
Defective B Cell Tolerance in Adenosine Deaminase Deficiency Is Corrected by Gene Therapy
Journal of Clinical Investigation
Medicine
Lentiviral Haemopoietic Stem/Progenitor Cell Gene Therapy for Treatment of Wiskott-Aldrich Syndrome: Interim Results of a Non-Randomised, Open-Label, Phase 1/2 Clinical Study
The Lancet Haematology
Hematology
Long-Term Follow Up of IPEX Syndrome Patients After Different Therapeutic Strategies: An International Multicenter Retrospective Study
Journal of Allergy and Clinical Immunology
Allergy
Immunology
In Vivo T-Cell Dynamics During Immune Reconstitution After Hematopoietic Stem Cell Gene Therapy in Adenosine Deaminase Severe Combined Immune Deficiency
Journal of Allergy and Clinical Immunology
Allergy
Immunology
288. Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatous Disease
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatosis
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Targeting Pre-Existing Anti-Transgene T Cell Response for Effective Gene Therapy of Mucopolysaccharidosis I in the Mouse Model of the Disease
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Challenges in Vector and Trial Design Using Retroviral Vectors for Long-Term Gene Correction in Hematopoietic Stem Cell Gene Therapy
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Expanded Circulating Hematopoietic Stem/Progenitor Cells as Novel Cell Source for the Treatment of TCIRG1 Osteopetrosis
Haematologica
Hematology
Autoimmune Dysregulation and Purine Metabolism in Adenosine Deaminase Deficiency
Frontiers in Immunology
Allergy
Immunology
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