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Publications by Brian K. Kaspar
AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study With a Prospective Natural History Cohort
Journal of Neuromuscular Diseases
Neurology
Gene Therapy for Duchenne Muscular Dystrophy
Archives of Neurology
Related publications
“The Times They Are A-Changin’.” in Reply to El-Zaidy Et Al.: AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study With a Prospective Natural History Cohort
Journal of Neuromuscular Diseases
Neurology
066 Avxs-101 Gene-Replacement Therapy (GRT) for Spinal Muscular Atrophy Type 1 (SMA1): Pivotal Phase 3 Study (STR1VE) Update
Journal of Neurology, Neurosurgery and Psychiatry
Psychiatry
Mental Health
Neurology
Surgery
Maintenance Factors for Persistence of Bulimic Pathology: A Prospective Natural History Study
International Journal of Eating Disorders
Psychiatry
Mental Health
EXPLORE: A Prospective, Multinational, Natural History Study of Patients With Acute Hepatic Porphyria With Recurrent Attacks
Hepatology
Medicine
Hepatology
014 AVXS-101 Gene-Replacement Therapy (GRT) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update
Journal of Neurology, Neurosurgery and Psychiatry
Psychiatry
Mental Health
Neurology
Surgery
Natural History of the Vascular Dementias: A Prospective Study of Seven Cases
Canadian Journal of Neurological Sciences
Medicine
Neurology
P.065 AVXS-101 Gene-Replacement Therapy (GRT)) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update
Canadian Journal of Neurological Sciences
Medicine
Neurology
Baseline Data of a Prospective Cohort Study: Cappadocia Cohort Study, Turkey
Türkiye Halk Sağlığı Dergisi
Age at Natural Menopause and Risk of Type 2 Diabetes: A Prospective Cohort Study
Diabetologia
Internal Medicine
Endocrinology
Metabolism
Diabetes
