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Publications by Jacqueline J. Glascock

Gene Therapy in Mouse Models of Spinal Muscular Atrophy :||Using SMN Gene Replacement to Address Biological Questions

English

Related publications

014 AVXS-101 Gene-Replacement Therapy (GRT) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update

Journal of Neurology, Neurosurgery and Psychiatry

English

P.065 AVXS-101 Gene-Replacement Therapy (GRT)) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update

Canadian Journal of Neurological Sciences

English

Psy16 - Health Outcome Improvements in Spinal Muscular Atrophy Type 1 Patients With Avxs-101 Gene Replacement Therapy

Value in Health

Occupational Health

English

Psy18 - Rapid Improvements in Motor Function in Spinal Muscular Atrophy Type 1 Following Avxs-101 Gene Replacement Therapy

Value in Health

Occupational Health

English

Muscle-Specific SMN Reduction Reveals Motor Neuron–independent Disease in Spinal Muscular Atrophy Models

Journal of Clinical Investigation

English

SMN Blood Levels in a Porcine Model of Spinal Muscular Atrophy

Journal of Neuromuscular Diseases

English

The Need for SMN-Independent Treatments of Spinal Muscular Atrophy (SMA) to Complement SMN-Enhancing Drugs

Frontiers in Neurology

English

Plasmid-Mediated Gene Therapy in Mouse Models of Limb Girdle Muscular Dystrophy

Molecular Therapy - Methods and Clinical Development

Molecular Medicine

Molecular Biology

English

066 Avxs-101 Gene-Replacement Therapy (GRT) for Spinal Muscular Atrophy Type 1 (SMA1): Pivotal Phase 3 Study (STR1VE) Update

Journal of Neurology, Neurosurgery and Psychiatry

English