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Publications by Luigi Naldini
Precise Gene Editing Preserves Hematopoietic Stem Cell Function Following Transient P53-Mediated DNA Damage Response
Cell Stem Cell
Molecular Medicine
Genetics
Cell Biology
Liver-Directed Lentiviral Gene Therapy in a Dog Model of Hemophilia B
Science Translational Medicine
Medicine
Lentiviral Haemopoietic Stem/Progenitor Cell Gene Therapy for Treatment of Wiskott-Aldrich Syndrome: Interim Results of a Non-Randomised, Open-Label, Phase 1/2 Clinical Study
The Lancet Haematology
Hematology
288. Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatous Disease
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Dual-Regulated Lentiviral Vector for Gene Therapy of X-Linked Chronic Granulomatosis
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
28. Intravenous Administration of Lentiviral Vectors Expressing Hyperactive Factor IX Converts Severe Into Mild Hemophilia B in a Canine Model
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Targeting Pre-Existing Anti-Transgene T Cell Response for Effective Gene Therapy of Mucopolysaccharidosis I in the Mouse Model of the Disease
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Challenges in Vector and Trial Design Using Retroviral Vectors for Long-Term Gene Correction in Hematopoietic Stem Cell Gene Therapy
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Dynamic Activity of miR-125b and miR-93 During Murine Neural Stem Cell Differentiation in Vitro and in the Subventricular Zone Neurogenic Niche
PLoS ONE
Multidisciplinary
