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Publications by Raili Riikonen
Native and Complexed IGF-1: Biodistribution and Pharmacokinetics in Infantile Neuronal Ceroid Lipofuscinosis
Journal of Drug Delivery
Rett Syndrome: Search for Prognostic Factors
Neurology and Neurobiology
Related publications
Infantile Neuronal Ceroid Lipofuscinosis
Pupillary Light Reflex Deficits in a Canine Model of Late Infantile Neuronal Ceroid Lipofuscinosis
Experimental Eye Research
Molecular Neuroscience
Ophthalmology
Sensory Systems
Cellular
Inducible Transgenic Expression of Tripeptidyl Peptidase 1 in a Mouse Model of Late-Infantile Neuronal Ceroid Lipofuscinosis
PLoS ONE
Multidisciplinary
Ovine Neuronal Ceroid Lipofuscinosis: A Large Animal Model Syntenic With the Human Neuronal Ceroid Lipofuscinosis Variant CLN6.
Journal of Medical Genetics
Genetics
Successful PGD for Late Infantile Neuronal Ceroid Lipofuscinosis Achieved by Combined Chromosome and TPP1 Gene Analysis
Reproductive BioMedicine Online
Gynecology
Reproductive Medicine
Developmental Biology
Obstetrics
Multifocal Retinopathy in Dachshunds With CLN2 Neuronal Ceroid Lipofuscinosis
Experimental Eye Research
Molecular Neuroscience
Ophthalmology
Sensory Systems
Cellular
Residual Levels of Tripeptidyl-Peptidase I Activity Dramatically Ameliorate Disease in Late-Infantile Neuronal Ceroid Lipofuscinosis
Molecular Genetics and Metabolism
Genetics
Molecular Biology
Biochemistry
Endocrinology
Metabolism
Diabetes
197. AAV2/5-Mediated Gene Therapy Synergizes With Bone Marrow Transplantation in the Treatment of Infantile Neuronal Ceroid Lipofuscinosis
Molecular Therapy
Molecular Medicine
Molecular Biology
Pharmacology
Medicine
Genetics
Drug Discovery
Neuronal Ceroid Lipofuscinosis Type 2: An Australian Case Series
Journal of Paediatrics and Child Health
Child Health
Pediatrics
Perinatology