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Publications by Thomas O Crawford

066 Avxs-101 Gene-Replacement Therapy (GRT) for Spinal Muscular Atrophy Type 1 (SMA1): Pivotal Phase 3 Study (STR1VE) Update

Journal of Neurology, Neurosurgery and Psychiatry

English

Assessment of Impaired Coordination Between Respiration and Deglutition in Children and Young Adults With Ataxia Telangiectasia

Developmental Medicine and Child Neurology

Developmental Neuroscience

English

Related publications

014 AVXS-101 Gene-Replacement Therapy (GRT) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update

Journal of Neurology, Neurosurgery and Psychiatry

English

P.065 AVXS-101 Gene-Replacement Therapy (GRT)) in Presymptomatic Spinal Muscular Atrophy (SMA): Study Update

Canadian Journal of Neurological Sciences

English

Psy16 - Health Outcome Improvements in Spinal Muscular Atrophy Type 1 Patients With Avxs-101 Gene Replacement Therapy

Value in Health

Occupational Health

English

Psy18 - Rapid Improvements in Motor Function in Spinal Muscular Atrophy Type 1 Following Avxs-101 Gene Replacement Therapy

Value in Health

Occupational Health

English

Spinal Muscular Atrophy Type 1

Pediatric Critical Care Medicine

Intensive Care Medicine

English

P.060 Time to Treatment Effect in Spinal Muscular Atrophy Type 1 (SMA1): An Indirect Comparison of Treatments

Canadian Journal of Neurological Sciences

English

AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study With a Prospective Natural History Cohort

Journal of Neuromuscular Diseases

English

Gene Therapy in Mouse Models of Spinal Muscular Atrophy :||Using SMN Gene Replacement to Address Biological Questions

English

Respiratory Management of the Infant With Type 1 Spinal Muscular Atrophy

Archives of Disease in Childhood

English